A small molecule is a small, chemically manufactured compound with a low molecular weight. Small molecule drugs help regulate a biological target such as an enzyme, channel or receptor to modify a disease process.
The large majority of drugs on the market today are small molecules and most are delivered orally. Small molecule drugs are part of what Syncona calls, the “First Wave” of technologies in healthcare and are dominated by large pharmaceutical companies.
Key facts
Unless stated all financials at 31 March 2023
£55m
Value of portfolio
5
Syncona Board seats
2
New investments in the year
The small molecule pipeline
Best ideas
Pre-clinical
Clinical
Late Clinical
BLA
Our domain areas
Syncona has deep domain expertise across four key therapeutic areas.